Realizing the Potential of Patient Organizations in Translational Research-Delivering Treatments for Rare Diseases 16/11/2018 Artículos
Record linkage between hospital discharges and mortality registries for motor neuron disease case ascertainment for the Spanish National Rare Diseases Registry 16/11/2018 Artículos
Regulatory considerations for developing drugs for rare diseases: orphan designations and early phase clinical trials 16/11/2018 Artículos
Renal replacement therapy for rare diseases affecting the kidney: an analysis of the ERA-EDTA Registry 16/11/2018 Artículos