Bayesian methods for the design and interpretation of clinical trials in very rare diseases 16/11/2018 Artículos
An automated communication system in a contact registry for persons with rare diseases: scalable tools for identifying and recruiting clinical research participants 16/11/2018 Artículos
An automated communication system in a Contact Registry for persons with rare diseases: tools for retaining potential clinical research participants 16/11/2018 Artículos
Aneurysm of the right sinus of Valsalva dissecting into the interventricular septum, submitral aneurysm and left ventricular non-compaction: three rare diseases in the same patient 16/11/2018 Artículos
Accelerating development, registration and access to medicines for rare diseases in the European Union through adaptive approaches: features and perspectives 16/11/2018 Artículos
Access to and quality of health and social care for rare diseases: patients’ and caregivers’ experiences 16/11/2018 Artículos
Access to information supporting availability of medicines for patients suffering from rare diseases looking for possible treatments: the EuOrphan Service 16/11/2018 Artículos
