Familial hemophagocytic lymphohistiocytosis: when rare diseases shed light on immune system functioning 16/11/2018 Artículos
Formalizing mappings to optimize automated schema alignment: application to rare diseases 16/11/2018 Artículos
Funding innovation for treatment for rare diseases: adopting a cost-based yardstick approach 16/11/2018 Artículos
Evidence and values: requirements for public reimbursement of drugs for rare diseases–a case study in oncology 16/11/2018 Artículos
Evidence-based medicine for rare diseases: implications for data interpretation and clinical trial design 16/11/2018 Artículos