Personalized drug discovery: HCA approach optimized for rare diseases at Tel Aviv University 16/11/2018 Artículos
Piedmont and Aosta Valley inter-regional network in the context of the Italian National Network for rare diseases 16/11/2018 Artículos
Opportunity Cost of Funding Drugs for Rare Diseases: The Cost-Effectiveness of Eculizumab in Paroxysmal Nocturnal Hemoglobinuria 16/11/2018 Artículos
Orphan drugs for rare diseases: is it time to revisit their special market access status? 16/11/2018 Artículos
Molecular genetic testing for ultra rare diseases: models for translation from the research laboratory to the CLIA-certified diagnostic laboratory 16/11/2018 Artículos
