Inaugural conference – what stakes face rare diseases in the French health care system 16/11/2018 Artículos
Inaugural conference: Progress made in the Second National Plan for Rare Diseases 16/11/2018 Artículos
Inborn errors of metabolism as rare diseases with a specific global situation [Los errores congénitos del metabolismo como enfermedades raras con un planteamiento global específico] 16/11/2018 Artículos
High cost drugs for rare diseases in Brazil: the case of lysosomal storage disorders 16/11/2018 Artículos