Current views on rare diseases research and orphan drugs development

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Resumen

Interest in rare diseases research and orphan drugs development has been increased distinctly in recent years. The number of affected people with rare diseases is considerable around the world and the formulation of national and international incentive policies to accelerate orphan drugs development, aiming at offering facilities and necessary conditions for patient access to treatment, gains favorable results. In particular, more measures should be taken to catalyze further progress due to behindhand level in this field in China. Additionally, therapeutic methods of rare diseases were also discussed.

Resumen realizado por los autores recogido de la publicación

Publicación

China:
Sheng Wu Gong Cheng Xue Bao = Chinese Journal Of Biotechnology,
2011

ISBN

Descripción física

724-729

Serie

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